Biogen Medical Research

Rare Diseases

Scientific Objectives

The following areas of research are currently being considered:

  • Friedreich’s Ataxia (FA): Biological, clinical, and patient-reported measures of disease – natural history and impacts to progression with modifying treatment.
  • Spinal Muscular Atrophy (SMA): Real-world effectiveness of nusinersen in teens and adults.

The following areas of research are currently not being considered:

  • Amyotrophic Lateral Sclerosis (ALS)

Research support is awarded on a highly competitive basis, and submission of research proposals in these areas of interest does not guarantee support will be awarded. 

We continuously strive to improve our submission process and provide necessary guidance to investigators.