Rare Diseases
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General Spinal Muscular Atrophy (SMA)
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The following areas of research are currently being considered to support studies related to Spinal Muscular Atrophy (SMA).
General SMA
- Natural history of teens and adults with SMA
Research support is awarded on a highly competitive basis, and submission of research proposals in these areas of interest does not guarantee that support will be awarded.
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- Nusinersen